16 Matching Annotations
  1. Last 7 days
  2. pmc.ncbi.nlm.nih.gov pmc.ncbi.nlm.nih.gov
    Long-term restoration of auditory function in a DFNA2 mouse model by adenine base editing
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    pmc.ncbi.nlm.nih.gov/articles/PMC13270111/
  3. Nov 2025
  4. pmc.ncbi.nlm.nih.gov pmc.ncbi.nlm.nih.gov
    Correction: Adenine base editing of CFTR using receptor targeted nanoparticles restores function to G542X cystic fibrosis airway epithelial cells
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    pmc.ncbi.nlm.nih.gov/articles/PMC12476327/
  5. Sep 2025
  6. www.sciencedirect.com www.sciencedirect.com
    A rare genetic variant confers resistance to neurodegeneration across multiple neurological disorders by augmenting selective autophagy
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    sciencedirect.com/science/article/pii/S0896627325006245
  7. www.nature.com www.nature.com
    A streamlined base editor engineering strategy to reduce bystander editing
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    nature.com/articles/s41467-025-63609-6
  8. Aug 2025
  9. pmc.ncbi.nlm.nih.gov pmc.ncbi.nlm.nih.gov
    PAM-flexible adenine base editing rescues hearing loss in a humanized MPZL2 mouse model harboring an East Asian founder mutation
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    pmc.ncbi.nlm.nih.gov/articles/PMC12325647/
  10. May 2025
  11. pmc.ncbi.nlm.nih.gov pmc.ncbi.nlm.nih.gov
    Systematic empirical evaluation of individual base editing targets: Validating therapeutic targets in USH2A and comparison of methods
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    pmc.ncbi.nlm.nih.gov/articles/PMC11997516/
  12. Feb 2025
  13. link.springer.com link.springer.com
    Massively parallel variant-to-function mapping determines functional regulatory variants of non-small cell lung cancer
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    link.springer.com/article/10.1038/s41467-025-56725-w
  14. Dec 2024
  15. www.sciencedirect.com www.sciencedirect.com
    Systematic identification of pathogenic variants of non-small cell lung cancer in the promoters of DNA-damage repair genes
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    sciencedirect.com/science/article/pii/S2352396424005164
  16. Sep 2024
  17. www.ncbi.nlm.nih.gov www.ncbi.nlm.nih.gov
    Engineering Oncogenic Hotspot Mutations on SF3B1 via CRISPR-Directed PRECIS Mutagenesis
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    ncbi.nlm.nih.gov/pmc/articles/PMC11421219/
  18. Aug 2024
  19. www.ncbi.nlm.nih.gov www.ncbi.nlm.nih.gov
    Genetically modified pigs with CD163 point mutation are resistant to HP-PRRSV infection
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    ncbi.nlm.nih.gov/pmc/articles/PMC11298667/
  20. Jun 2024
  21. www.ncbi.nlm.nih.gov www.ncbi.nlm.nih.gov
    Development and testing of a versatile genome editing application reporter (V-GEAR) system
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    ncbi.nlm.nih.gov/pmc/articles/PMC11101715/
  22. Jul 2023
  23. www.sciencedirect.com www.sciencedirect.com
    Multi-level functional genomics reveals molecular and cellular oncogenicity of patient-based 3′ untranslated region mutations
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    sciencedirect.com/science/article/pii/S2211124723008513
  24. Mar 2023
  25. www.sciencedirect.com www.sciencedirect.com
    Human T cell generation is restored in CD3δ severe combined immunodeficiency through adenine base editing
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    sciencedirect.com/science/article/pii/S0092867423001708
  26. Dec 2022
  27. aacrjournals.org aacrjournals.org
    Efficient Correction of Oncogenic KRAS and TP53 Mutations through CRISPR Base Editing
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    aacrjournals.org/cancerres/article/82/17/3002/708290/Efficient-Correction-of-Oncogenic-KRAS-and-TP53
  28. Mar 2022
  29. www.ncbi.nlm.nih.gov www.ncbi.nlm.nih.gov
    RNAi-Mediated Screen of Primary AML Cells Nominates MDM4 as a Therapeutic Target in NK-AML with DNMT3A Mutations
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    ncbi.nlm.nih.gov/pmc/articles/PMC8909053/
  30. May 2021
  31. www.sciencedirect.com www.sciencedirect.com
    Adenine base editing and prime editing of chemically derived hepatic progenitors rescue genetic liver disease
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    sciencedirect.com/science/article/pii/S1934590921001673