Patient 1
Case#: Patient 1, Male, 3 years (report),
DiseaseAssertion: Hurler Syndrome
FamilyInfo: N/A
CasePresentingHPOs: HP:0003593, HP:0001249, HP:0001510 (Infantile Onset, Mental Retardation (Severe), Growth Retardation)
CaseHPOFreeText: Organomegaly (Severe), Bone Involvement
CaseNotHPOs: N/A
CaseNotHPOFreeText: N/A
CaseEnzymeAssay: 0 Leukocyte IDUA Activity μKat/Kg Protein
CaseUrineGAGs: N/A
CaseERT: N/A
**CaseBMT: ** N/A
GenotypingMethod: Not Provided
Variant1: c.1650+1G>T
Variant1ClinVarID: 1323092
Variant1CAID: CA355965141
Variant2: c.1650+1G>T
Variant2ClinVarID: 1323092
Variant2CAID: CA355965141
** AdditionalVariants:** N/A
ParentalGenotype: Both parents had the c.1650 + 1G > T variant on Allele 1, but were normal on Allele 2
PreviouslyPublished: N/A