5 mg/kg (N = 3)
Case1HPOsFreeText: 5 mg/kg GAA treatment, GAA activity at 2 pmol/punch/hr, GAA activity at 6% lower limit of normal
CaseAddInfo: Late Onset Pompe Disease
5 mg/kg (N = 3)
Case1HPOsFreeText: 5 mg/kg GAA treatment, GAA activity at 2 pmol/punch/hr, GAA activity at 6% lower limit of normal
CaseAddInfo: Late Onset Pompe Disease