6 Matching Annotations
  1. Last 7 days
    1. Supplementary Tables 1 and 2 combined information:

      Case18: Gt18, Male, 20 years old

      DiseaseAssertion: Glanzmann thrombasthenia

      FamilyInfo: Available per Table 1; however, very minimal information

      ParentalGenotype: Parents are consanguineous, no other genotype information available

      CasePresentingHPOs: HP:0000421

      (Epistaxis)

      CaseHPOFreeText: N/A

      CaseNotHPOs: N/A

      CaseNotHPOsFreeText: N/A

      ProteinExpression: Showed <5% of αIIbβ3 expression measured by flow cytometry

      PlateletAggregation: Platelet aggregation showed no response to ADP and collagen but normal response to ristocetin

      CasePreviousTesting: All exons from ITGA2B and ITGB3 genes were amplified by PCR using intronic primers. DNA sequencing was determined by Sanger sequencing.

      Gene: ITGA2B

      Variant: NM_000419.3:c.2671C>T (p.Gln891Ter)

      LegacyVariant: N/A

      ClinVar: N/A

      CAiD: CA8602626 (p.Gln891Ter)

      gnomAD: N/A

    2. Supplementary Tables 1 and 2 combined information:

      Case17a: GT17a, Female, 14 years old, sister of GT17b proband

      DiseaseAssertion: Glanzmann thrombasthenia

      FamilyInfo: Available per supplementary table 1

      ParentalGenotype: Parents are not consanguineous, no other genotype information available

      CasePresentingHPOs: HP:0000978, HP:0000979, HP:0031364, HP:0000421

      (Bruising, purpura, ecchymosis, epistaxis)

      CaseHPOFreeText: Post traumatic hemorrhage

      CaseNotHPOs: N/A

      CaseNotHPOsFreeText: N/A

      ProteinExpression: Showed <5% of αIIbβ3 expression measured by flow cytometry

      PlateletAggregation: Platelet aggregation showed a small response to ADP and collagen but normal response to ristocetin

      CasePreviousTesting: All exons from ITGA2B and ITGB3 genes were amplified by PCR using intronic primers. DNA sequencing was determined by Sanger sequencing.

      Gene: ITGA2B

      Variant: NM_000419.3:c.799+2T>C and NM_000419.3:c.2671C>T (p.Gln891Ter)

      LegacyVariant: N/A

      ClinVar: N/A

      CAiD: CA399805155 (c.799 +2 T>C) and CA8602626 (p.Gln891Ter)

      gnomAD: N/A

    3. Supplementary Tables 1 and 2 combined information:

      Case26: GT26, Male, 13 years old

      DiseaseAssertion: Glanzmann thrombasthenia

      FamilyInfo: Not available per supplementary table 1

      ParentalGenotype: Parents are not consanguineous, no other genotype information available

      CasePresentingHPOs: HP:0000978, HP:0000979, HP:0031364

      (Bruising, purpura, ecchymosis)

      CaseHPOFreeText: N/A

      CaseNotHPOs: N/A

      CaseNotHPOsFreeText: N/A

      ProteinExpression: Showed <5% of αIIbβ3 expression measured by flow cytometry

      PlateletAggregation: Platelet aggregation showed no response to ADP and collagen but normal response to ristocetin

      CasePreviousTesting: All exons from ITGA2B and ITGB3 genes were amplified by PCR using intronic primers. DNA sequencing was determined by Sanger sequencing.

      Gene: ITGA2B

      Variant: NM_000419.3:c.2333A>C (Gln778Pro) and NM_000419.3:c.2671C>T (p.Gln891Ter)

      LegacyVariant: N/A

      ClinVar: 225393 (p.Gln778Pro)

      CAiD: CA290947544 (p.Gln778Pro) and CA8602626 (p.Gln891Ter)

      gnomAD: MAF in East Asian population: 0.0001087 https://gnomad.broadinstitute.org/variant/17-42453691-T-G

    4. Supplementary Tables 1 and 2 combined information:

      Case4: GT4, Female, 22 years old

      DiseaseAssertion: Glanzmann thrombasthenia

      FamilyInfo: Not available per supplementary table 1

      ParentalGenotype: Parents are consanguineous, no other genotype information available

      CasePresentingHPOs: HP:0000978, HP:0000979, HP:0031364, HP:0000421, HP:0000225, HP:0000132

      (Bruising, purpura, ecchymosis, epistaxis, gingival bleeding, menorrhagia)

      CaseHPOFreeText: N/A

      CaseNotHPOs: N/A

      CaseNotHPOsFreeText: N/A

      ProteinExpression: Showed <5% of αIIbβ3 expression measured by flow cytometry

      PlateletAggregation: Platelet aggregation showed no response to ADP and collagen but normal response to ristocetin

      CasePreviousTesting: All exons from ITGA2B and ITGB3 genes were amplified by PCR using intronic primers. DNA sequencing was determined by Sanger sequencing.

      Gene: ITGA2B

      Variant: NM_000419.3:c.2671C>T (p.Gln891Ter)

      LegacyVariant: N/A

      ClinVar: N/A

      CAiD: CA8602626

      gnomAD: N/A

    1. patient 8

      Case#: Patient 8

      DiseaseAssertion: Glanzmann thrombasthenia

      FamilyInfo: Not provided

      ParentalGenotype: Not provided

      CasePresentingHPOs: (HP:0000421, Epistaxis)

      PlateletAggregation: All patients had abnormal platelet aggregation studies prompting analysis of platelet glycoprotein expression by flow cytometry.

      ProteinExpression: Flow cytometry, 11 of 12 patients with GT had reduced antibody binding to GPIIb/IIIa

      CasePreviousTesting: Not provided

      PreviouslyPublished: Not provided

      Gene: ITGA2B

      Variant: c.1750C>T, p. (R584X)

      HGVS: NM_000419.5:c.1750C>T

      ClinVar: 2892 https://www.ncbi.nlm.nih.gov/clinvar/variation/2892/

      CAID: CA115834

      gnomAD: PopMax = 0.00008834 https://gnomad.broadinstitute.org/variant/17-44380004-G-A?dataset=gnomad_r4

      Variant: c.2671C>T, p. (Q891X)

      HGVS: NM_000419.5:c.2671C>T

      ClinVar: 953054 https://www.ncbi.nlm.nih.gov/clinvar/variation/953054/

      CAID: CA8602626

      gnomAD: PopMax = 0.000007390 https://gnomad.broadinstitute.org/variant/17-44375647-G-A?dataset=gnomad_r4

    1. Nonsense-mediated mRNA decay efficiency influencesbleeding severity inITGA2Bc.2659C > T (p.Q887X)knock-in mice

      PMID: 33928629

      Previously annotated and reported Probands: PMID: 29675921. New Functional Evidence.

      CAID: CA8602626

      Gene: ITGA2B

      Variant: NM_000419.3:c.2671C>T (p.Gln891Ter)

      FunctionalEvidence: For Q887X mutation: Knock-in mice generated using CRISPR/Cas9 displaed no spontaneous bleeding phenotypes. Platelet morphology cofirmed to be normal and comparable platelet numbers to WT mice. Mean bleeding time increased and platelet aggregation impaired compared to WT. ITGA2B mRNA levels low in KI mice.